Agenda

NERDS 2025 Workshop Tentative Agenda

Day 1, Thursday, October 9th 2025 (Location: )

  • 8:30 AM - 10:00 AM: Keynote Session 1
    • 8:30 AM - 9:00 AM: Speaker 1: Carmen Bozic, Chief Medical Officer, Vertex Pharmaceutical
    • 9:00 AM - 9:30 AM: Speaker 2: Jonathan G. Seidman, Harvard Medical School
    • 9:30 AM - 10:00 AM: Discussion and Q&A Session: Lee-Jen Wei, Harvard T.H. Chan School of Public Health
  • 10:30 AM - 12:10 PM: Session 1: Innovative Design and Methods in Rare Diseases
  • 1:10 PM - 3:00 PM: Session 2: Gene and Cell Therapy
  • 3:30 PM – 4:50 PM: Session 3: AI and Machine Learnings
  • 5:00 PM - 6:00 PM: Poster Session

Day 2, Friday, October 10th 2025 (Location: )

  • 8:30 AM - 10:00 AM: Keynote Session 2
    • 8:30 AM - 9:00 AM: Speaker 1: Dr. Mark Van Der Laan, UC Berkeley
    • 9:00 AM - 9:30 AM: Speaker 2: Edward Neilan, Chief Medical and Scientific Officer, National Organization for Rare Disorders (NORD)
    • 9:30 AM - 10:00 AM: Discussion and Q&A Session: Li Wang, Head of Statistical Innovation group, AbbVie
  • 10:30 AM - 12:10 PM: Session 4: Real-world evidence and HTA